- Spinal Muscular Atrophy Insights
- Posts
- Spinal Muscular Atrophy Insights
Spinal Muscular Atrophy Insights
Understanding spinal muscular atrophy: a guide for patients
Exclusive ReportUnderstanding spinal muscular atrophy: a guide for patients This week, we're featuring a brand-new guide on SMA, created with AllMyHealth. Whether you're newly diagnosed, a caregiver, or looking for reliable information, this resource covers symptoms, diagnosis, treatment options, and support networks - all in one place. View the Full ReportThe report is available for free online on the AllMyHealth website. www.allmyhealth.io/report ![]() |
Top StoriesScholar Rock Submits Apitegromab Application to FDAApitegromab, a new therapy, may help improve strength and function for people with SMA by targeting muscle growth. Scholar Rock's application seeks approval for this treatment. Read More →Activists Seek Lower SMA Medicine CostsPatients with Spinal Muscular Atrophy face high treatment costs, prompting activists to urge the government to allow generic production of the medicine Risdiplam to reduce prices. Read More → |
Latest Research A recent study led by Nie et al. (2025) has explored how spinal muscular atrophy (SMA) types 2 and 3 affect the brain's white matter. White matter consists of nerve fibers that connect different parts of the brain, facilitating communication between them. The researchers used advanced MRI techniques to examine the brains of children diagnosed with SMA types 2 and 3. They discovered that these children had reduced integrity in their white matter, meaning the connections between different brain regions were not as robust as those in children without SMA. This reduction in white matter integrity suggests that SMA may impact not only motor functions but also the brain's overall network connectivity. |