Breakthroughs in SMA gene therapy and safety, and personalised treatments and early intervention.
Exploring caregivers' needs and advancements in SMA treatments and research.
Advancements in research, awareness initiatives, and new tools for understanding and managing SMA.
Latest insights covering murine models, disease modifiers, and therapeutic innovations reveal significant advancements in the understanding and treatment of SMA.
Brain abnormalities linked to SMA, advancements in treatment and care strategies, and inspiring stories of patients and advocates driving awareness and support for this rare disease.
Recent studies unveil critical brain abnormalities linked to SMA, advances in higher-dose nusinersen treatment, and insights into scoliosis risk factors.
